Open AccessNon-invasive and allele-specific silencing therapy for Polyglutamine disorders: the case of Machado-Joseph disease/Spinocerebellar ataxia type 3
Author(s) -
Rui Jorge Nobre,
Joana Saraiva,
Susana Paixão,
Cellia Fusco,
Magda M. Santana,
Catarina Oliveira Miranda,
Lorena Petrella,
José Sereno,
João Castelhano,
Miguel CasteloBranco,
Miguel SenaEsteves,
Luís Pereira de Almeida
Publication year - 2019
Publication title -
frontiers in cellular neuroscience
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 1.877
H-Index - 86
ISSN - 1662-5102
DOI - 10.3389/conf.fncel.2019.01.00007
Subject(s) - spinocerebellar ataxia , machado–joseph disease , gene silencing , trinucleotide repeat expansion , biology , rna interference , viral vector , ataxia , genetics , virology , allele , neuroscience , rna , gene , recombinant dna
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