Open AccessClinical outcomes in idursulfase-treated patients with mucopolysaccharidosis type II: 3-year data from the hunter outcome survey (HOS)
Author(s) -
Joseph Muenzer,
Roberto Giugliani,
Maurizio Scarpa,
Anna TylkiSzymańska,
Virginie Jego,
Michael Beck
Publication year - 2017
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/v7sw-r464
Subject(s) - mucopolysaccharidosis type ii , hunter syndrome , medicine , mucopolysaccharidosis , outcome (game theory) , pediatrics , psychology , enzyme replacement therapy , disease , mathematics , mathematical economics