Open AccessA phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II
Author(s) -
Joseph Muenzer,
Christian J. Hendriksz,
Zheng Fan,
Suresh Vijayaraghavan,
V. Hugh Perry,
Saikat Santra,
Guirish A. Solanki,
Mary Ann Mascelli,
Lei Pan,
Nan Wang,
Kenneth Sciarappa,
Ann Barbier
Publication year - 2016
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/smtj-kk84
Subject(s) - intrathecal , mucopolysaccharidosis type ii , mucopolysaccharidosis , hunter syndrome , medicine , phase (matter) , mucopolysaccharidosis i , pediatrics , enzyme replacement therapy , anesthesia , disease , chemistry , organic chemistry