Open AccessNeurological Correction of Lysosomal Storage in a Mucopolysaccharidosis IIIB Mouse Model by Adeno-associated Virus-Mediated Gene Delivery
Author(s) -
Haixia Fu,
R. Jude Samulski,
Thomas J. McCown,
Yoana J. Picornell,
David F. Fletcher,
Joseph Muenzer
Publication year - 2002
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/rm0s-cp46
Subject(s) - mucopolysaccharidosis , adeno associated virus , gene delivery , virology , lysosomal storage disease , lysosomal storage disorders , gene , genetic enhancement , medicine , biology , genetics , pathology , vector (molecular biology) , disease , recombinant dna