
Targeted correction of a thalassemia-associated -globin mutation induced by pseudo-complementary peptide nucleic acids
Author(s) -
Pallavi Lonkar,
KiHyun Kim,
Jean Y. Kuan,
James Chin,
Faye A. Rogers,
Melissa Knauert,
Ryszard Kole,
Peter E. Nielsen,
Peter M. Glazer
Publication year - 2009
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/kt3a-9623
Subject(s) - thalassemia , nucleic acid , globin , mutation , genetics , chemistry , biology , gene