Open AccessIntrathecal administration of AAV/GALC vectors in 10-11-day-old twitcher mice improves survival and is enhanced by bone marrow transplant: Intrathecal AAV Combined With BMT To Treat Krabbe Disease
Author(s) -
Subha KarumuthilMelethil,
M. Scott Marshall,
Clifford Heindel,
Benas Jakubauskas,
Ernesto R. Bongarzone,
Steven J. Gray
Publication year - 2016
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/k41h-ea43
Subject(s) - intrathecal , krabbe disease , medicine , bone marrow , bone marrow transplant , bone marrow transplantation , disease , anesthesia , pathology , leukodystrophy