
An AAV9 coding for frataxin clearly improved the symptoms and prolonged the life of Friedreich ataxia mouse models
Author(s) -
Catherine Gérard,
Xiao Xiao,
Mohammed Filali,
Zoé Coulombe,
Marie Arsenault,
Jacques Couët,
Juan Li,
MarieClaude Drolet,
Pierre Chapdelaine,
Amina Chikh,
Jacques P. Tremblay
Publication year - 2014
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/5dy9-rz84
Subject(s) - frataxin , ataxia , coding (social sciences) , biology , neuroscience , psychology , genetics , gene , iron binding proteins , sociology , social science