
Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors
Author(s) -
Denise E. Sabatino,
Amy M. Lange,
Ekaterina Altynova,
Rita Sarkar,
Shangzhen Zhou,
Elizabeth P. Merricks,
Helen Franck,
Timothy C. Nichols,
Valder R. Arruda,
Haig H. Kazazian
Publication year - 2011
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/1e0d-x685
Subject(s) - genetic enhancement , medicine , term (time) , virology , intensive care medicine , gene , biology , genetics , physics , quantum mechanics