
Enzyme replacement therapy at reduced doses in pediatric patients with Gaucher disease type 1: a systematic review
Author(s) -
A.O. Ryzhov,
V. K. Fedyaeva
Publication year - 2020
Publication title -
medicinskie tehnologii. ocenka i vybor
Language(s) - English
Resource type - Journals
eISSN - 2712-7877
pISSN - 2219-0678
DOI - 10.17116/medtech20204204175
Subject(s) - enzyme replacement therapy , medicine , disease , glucocerebrosidase , gaucher's disease , pediatrics