EFFICACY AND SAFETY OF ENZYME REPLACEMENT THERAPY IN CHILDREN WITH MUCOPOLYSACCHARIDOSIS TYPE I, II, AND VI: A SINGLE-CENTER COHORT STUDY
Author(s) -
Л. А. Осипова,
Ludmila M. Kuzenkova,
Leyla S. Namazova-Baranova,
А. K. Gevorkyan,
Tatiana V. Podkletnova,
Nikolay Mayanskiy,
Grigory V. Revunenkov,
Nato D. Vashakmadze
Publication year - 2018
Publication title -
вопросы современной педиатрии
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.12
H-Index - 5
eISSN - 1682-5535
pISSN - 1682-5527
DOI - 10.15690/vsp.v17i1.1858
Subject(s) - enzyme replacement therapy , medicine , excretion , mucopolysaccharidosis type ii , adverse effect , creatinine , cohort , urine , urinary system , hunter syndrome , urology , pediatrics , disease
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