Open AccessEFFICACY AND SAFETY OF ENZYME REPLACEMENT THERAPY IN CHILDREN WITH MUCOPOLYSACCHARIDOSIS TYPE I, II, AND VI: A SINGLE-CENTER COHORT STUDY
Author(s) -
Liliya A. Osipova,
Л.М. Кузенкова,
Л. С. Намазова-Баранова,
А. К. Геворкян,
Tatyana V. Podkletnova,
Н. А. Маянский,
Г. В. Ревуненков,
Nato D. Vashakmadze
Publication year - 2018
Publication title -
voprosy sovremennoj pediatrii
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.12
H-Index - 5
eISSN - 1682-5535
pISSN - 1682-5527
DOI - 10.15690/vsp.v17i1.1858
Subject(s) - enzyme replacement therapy , medicine , excretion , mucopolysaccharidosis type ii , adverse effect , creatinine , cohort , urine , urinary system , hunter syndrome , urology , pediatrics , disease