Optogenetic modeling of human neuromuscular circuits in Duchenne muscular dystrophy with CRISPR and pharmacological corrections
Author(s) -
Amaia ParedesRedondo,
Peter Harley,
Eleni Maniati,
David Ryan,
Sandra Louzada,
Jinhong Meng,
Anna Kowala,
Beiyuan Fu,
Fengtang Yang,
Pentao Liu,
Silvia Marino,
Olivier Pourquié,
Francesco Muntoni,
Jun Wang,
Ivo Lieberam,
YungYao Lin
Publication year - 2021
Publication title -
science advances
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 5.928
H-Index - 146
ISSN - 2375-2548
DOI - 10.1126/sciadv.abi8787
Subject(s) - duchenne muscular dystrophy , neuromuscular junction , optogenetics , dystrophin , muscular dystrophy , neuroscience , biology , motor neuron , neuromuscular disease , crispr , microbiology and biotechnology , medicine , gene , genetics , disease , spinal cord
Description
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