
A phase I/IIa double blind single institute trial of low dose sirolimus for Pendred syndrome/DFNB4
Author(s) -
Masato Fujioka,
Takumi Akiyama,
Makoto Hosoya,
Kayoko Kikuchi,
Yuto Fujiki,
Yasuko Saito,
Keisuke Yoshihama,
Hiroyuki Ozawa,
Keita Tsukada,
Shinya Nishio,
Shin Ichi Usami,
Tatsuo Matsunaga,
Tomonobu Hasegawa,
Yasunori Sato,
Kaoru Ogawa
Publication year - 2020
Publication title -
medicine
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.59
H-Index - 148
eISSN - 1536-5964
pISSN - 0025-7974
DOI - 10.1097/md.0000000000019763
Subject(s) - medicine , tolerability , placebo , adverse effect , hearing loss , dosing , audiology , pathology , alternative medicine
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