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P‐055: TRIAL IN PROGRESS: A PHASE 2, OPEN‐LABEL STUDY EVALUATING THE SAFETY AND EFFICACY OF THE ERYTHROCYTE PYRUVATE KINASE ACTIVATOR ETAVOPIVAT IN PATIENTS WITH THALASSEMIA OR SICKLE CELL DISEASE
Author(s) -
T. COATES,
A. LAL,
R. BROWN,
T. KALFA,
J. KWIATKOWSKI,
J. BREVARD,
C. TRENOR,
K. WOOD,
S. SHETH
Publication year - 2022
Publication title -
hemasphere
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.677
H-Index - 11
ISSN - 2572-9241
DOI - 10.1097/01.hs9.0000873112.02265.19
Subject(s) - medicine , thalassemia , hemolysis , pyruvate kinase , anemia , pyruvate kinase deficiency , ineffective erythropoiesis , cohort , sickle cell anemia , beta thalassemia , hemolytic anemia , gastroenterology , disease , erythropoiesis , glycolysis , metabolism

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