Open AccessP1735: IMPROVEMENTS IN PATIENT‐REPORTED OUTCOMES IN MITAPIVAT‐TREATED PATIENTS WITH PYRUVATE KINASE DEFICIENCY: A DESCRIPTIVE ANALYSIS FROM THE PHASE 3 ACTIVATE TRIAL
Author(s) -
Kuo K. H.,
Grace R. F.,
Beers E. J.,
Barcellini W.,
Glenthøj A.,
Holzhauer S.,
Patel P.,
Bey V.,
Li J.,
Zagadailov E.,
AlSamkari H.
Publication year - 2022
Publication title -
hemasphere
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.677
H-Index - 11
ISSN - 2572-9241
DOI - 10.1097/01.hs9.0000849796.83034.ba
Subject(s) - medicine , pyruvate kinase deficiency , placebo , anemia , clinical endpoint , hemolysis , randomized controlled trial , jaundice , quality of life (healthcare) , pediatrics , pyruvate kinase , gastroenterology , glycolysis , metabolism , alternative medicine , nursing , pathology