
P1565: MITAPIVAT IMPROVES INEFFECTIVE ERYTHROPOIESIS AND REDUCES IRON OVERLOAD IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY
Author(s) -
Beers E. J.,
AlSamkari H.,
Grace R. F.,
Barcellini W.,
Glenthøj A.,
Judge M. P.,
Kosinski P. A.,
Xu R.,
Bey V.,
McGee B.,
Porter J. B.,
Kuo K. H. M.
Publication year - 2022
Publication title -
hemasphere
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.677
H-Index - 11
ISSN - 2572-9241
DOI - 10.1097/01.hs9.0000849116.94935.15
Subject(s) - medicine , pyruvate kinase deficiency , soluble transferrin receptor , ineffective erythropoiesis , anemia , erythropoiesis , transferrin saturation , ferritin , iron deficiency , hepcidin , hemolysis , gastroenterology , erythropoietin , pyruvate kinase , metabolism , glycolysis , iron status