Open AccessRisdiplam in Type 1 Spinal Muscular Atrophy
Author(s) -
Giovanni Baranello,
Basil T. Darras,
John Day,
Nicolas Deconinck,
Andrea Klein,
Riccardo Masson,
Eugenio Mercuri,
Kristy Rose,
Muna El-Khairi,
Marianne Gerber,
Ksenija Gorni,
Omar Khwaja,
H. Kletzl,
R. Scalco,
Timothy J. Seabrook,
Paulo Fontoura,
Laurent Servais
Publication year - 2021
Publication title -
new england journal of medicine
Language(s) - Uncategorized
Resource type - Journals
SCImago Journal Rank - 19.889
H-Index - 1030
eISSN - 1533-4406
pISSN - 0028-4793
DOI - 10.1056/nejmoa2009965
Subject(s) - spinal muscular atrophy , medicine , physical medicine and rehabilitation , anatomy , pathology , disease
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