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O4‐05‐02: THE INVESTIGATIONAL STEREOPURE ANTISENSE OLIGONUCLEOTIDE WVE‐3972‐01 PREFERENTIALLY REDUCES G 4 C 2 REPEAT‐CONTAINING C9ORF72 TRANSCRIPTS: A POTENTIAL THERAPEUTIC APPROACH FOR THE TREATMENT OF FRONTOTEMPORAL DEMENTIA
Author(s) -
Dodart Jean-Cosme,
Liu Yuanjing,
Tran Helene,
Berkovitch Shaunna,
Byrne Michael,
Durbin Ann,
Iwamoto Naoki,
Jang Hyun Gyung,
Kandasamy Pachamuthu,
Liu Fangjun,
Mohapatra Susovan,
Yang Hailin,
Yin Yuan,
Zhang Jason,
Zhong Zhong,
Vargeese Chandra,
Brown Robert H.
Publication year - 2018
Publication title -
alzheimer's and dementia
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 6.713
H-Index - 118
eISSN - 1552-5279
pISSN - 1552-5260
DOI - 10.1016/j.jalz.2018.06.2934
Subject(s) - trinucleotide repeat expansion , c9orf72 , microbiology and biotechnology , reporter gene , rna , gene , oligonucleotide , induced pluripotent stem cell , chemistry , transgene , mutant , biology , gene expression , biochemistry , allele , embryonic stem cell