Open AccessLong-Term Neuropsychological Outcomes from an Open-Label Phase I/IIa Trial of 2-Hydroxypropyl-β-Cyclodextrins (VTS-270) in Niemann-Pick Disease, Type C1
Author(s) -
Cristan Farmer,
Audrey Thurm,
Nicole Y. Farhat,
Simona Bianconi,
Lee Ann Keener,
Forbes D. Porter
Publication year - 2019
Publication title -
cns drugs
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 1.565
H-Index - 108
eISSN - 1179-1934
pISSN - 1172-7047
DOI - 10.1007/s40263-019-00642-2
Subject(s) - neuropsychology , niemann–pick disease, type c , medicine , neuropsychological assessment , psychology , pediatrics , disease , cognition , psychiatry
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