
Impact of hematologic complete response in the treatment of sporadic late‐onset nemaline myopathy associated with monoclonal gammopathy
Author(s) -
Maia Tânia,
Bergantim Rui,
Costa Henrique,
Pinheiro Jorge,
Trigo Fernanda
Publication year - 2021
Publication title -
clinical case reports
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.21
H-Index - 9
ISSN - 2050-0904
DOI - 10.1002/ccr3.4471
Subject(s) - nemaline myopathy , medicine , monoclonal gammopathy of undetermined significance , monoclonal gammopathy , gammopathy , myopathy , paraproteinemias , pathology , monoclonal , immunology , monoclonal antibody , antibody
Monoclonal gammopathy of undetermined significance (MGUS) may be associated with pathologies with severe neuromuscular manifestations such as sporadic late‐onset nemaline myopathy (SLONM). We describe a difficult to diagnose case of SLNOM with marked clinical improvement after achieving gammopathy complete hematologic response.