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Targeting splicing in spinal muscular atrophy
Author(s) -
Burnett Barrington G.,
Sumner Charlotte J.
Publication year - 2008
Publication title -
annals of neurology
Language(s) - Uncategorized
Resource type - Journals
SCImago Journal Rank - 4.764
H-Index - 296
eISSN - 1531-8249
pISSN - 0364-5134
DOI - 10.1002/ana.21305
Subject(s) - smn1 , spinal muscular atrophy , sma* , exon , biology , genetics , gene , motor neuron , alternative splicing , rna splicing , gene dosage , gene expression , neuroscience , rna , spinal cord , mathematics , combinatorics

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