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Position statement: National Gaucher Foundation Medical Advisory Board, January 7, 2014
Author(s) -
Barranger John A.,
Brady Roscoe O.,
Grabowski Gregory A.,
Mankin Henry,
Mistry Pramod K.,
Weinreb Neal J.
Publication year - 2014
Publication title -
american journal of hematology
Language(s) - Uncategorized
Resource type - Journals
SCImago Journal Rank - 2.456
H-Index - 105
eISSN - 1096-8652
pISSN - 0361-8609
DOI - 10.1002/ajh.23687
Subject(s) - medicine , enzyme replacement therapy , observational study , hepatosplenomegaly , clinical trial , disease , pediatrics