Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy
Author(s) -
Michela Guglieri,
Kate Bushby,
Michael McDermott,
P. Morehart,
Rabi Tawil,
William B. Martens,
Barbara E. Herr,
Elaine McColl,
Chris Speed,
Jennifer Wilkinson,
Janbernd Kirschner,
Wendy King,
Michelle Eagle,
Mary W. Brown,
Tracey Willis,
Robert C. Griggs,
Volker Straub,
Henriette van Ruiten,
AnneMarie Childs,
Emma Ciafaloni,
Perry B. Shieh,
Stefan Spinty,
Lorenzo Maggi,
Giovanni Baranello,
Russell J. Butterfield,
Iain Horrocks,
Helen Roper,
Z. Alhaswani,
Kevin M. Flanigan,
Nancy L. Kuntz,
Adnan Manzur,
Basil T. Darras,
Peter B. Kang,
Leslie Morrison,
Monika KrzesniakSwinarska,
Jean K. Mah,
Tiziana Mongini,
Federica Ricci,
Maja von der Hagen,
Richard S. Finkel,
Kathleen O’Reardon,
Matthew Wicklund,
Ashutosh Kumar,
Craig M. McDonald,
Jay J. Han,
Nanette C. Joyce,
Erik Henricson,
Ulrike ScharaSchmidt,
Andrea Gangfuß,
Ekkehard Wilichowski,
Richard J. Barohn,
Jeffrey Statland,
Craig Campbell,
Giuseppe Vita,
Gian Luca Vita,
James F. Howard,
Imelda Hughes,
Hugh J. McMillan,
Elena Pegoraro,
Luca Bello,
W. Bryan Burnette,
Mathula Thangarajh,
Taeun Chang
Publication year - 2022
Publication title -
jama
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 4.688
H-Index - 680
eISSN - 1538-3598
pISSN - 0098-7484
DOI - 10.1001/jama.2022.4315
Subject(s) - medicine , duchenne muscular dystrophy , dosing , corticosteroid , muscular dystrophy , pediatrics , physical therapy , physical medicine and rehabilitation
Corticosteroids improve strength and function in boys with Duchenne muscular dystrophy. However, there is uncertainty regarding the optimum regimen and dosage.
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