an exon skipping strategy using AAV8-U7snRNA vectors for the treatment of Duchenne muscular dystrophy - results in GRMD dogs and clinical perspectives.
Author(s) -
Caroline C. Le Guiner,
M. Montus,
L. Servais,
Luis Garcı́a,
Yves Fromes,
JeanYves Hogrel,
Pierre Carlier,
Yan Y. Cherel,
P. Moullier,
T. Voit
Publication year - 2012
Publication title -
hal (le centre pour la communication scientifique directe)
Language(s) - English
Resource type - Conference proceedings
Subject(s) - duchenne muscular dystrophy , medicine , muscular dystrophy , exon skipping , exon , biology , genetics , gene , alternative splicing
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