Open Accessan exon skipping strategy using AAV8-U7snRNA vectors for the treatment of Duchenne muscular dystrophy - results in GRMD dogs and clinical perspectives.
Author(s) -
Caroline Le Guiner,
M. Montus,
Laurent Servais,
Luis Garcı́a,
Y. Fromes,
JeanYves Hogrel,
Pierre Carlier,
Yan Chérel,
Philippe Moullier,
Thomas Voït
Publication year - 2012
Publication title -
hal (le centre pour la communication scientifique directe)
Language(s) - English
Resource type - Conference proceedings
Subject(s) - duchenne muscular dystrophy , medicine , muscular dystrophy , exon skipping , exon , biology , genetics , gene , alternative splicing