Open AccessMethodological challenges in monitoring new treatments for rare diseases: lessons from the cryopyrin-associated periodic syndrome registry
Author(s) -
Hugh A. Tilson,
Paola Primatesta,
Dennis Kim,
Barbara Rauer,
Philip N. Hawkins,
Hal M. Hoffman,
Jasmin KuemmerleDeschner,
Tom van der Poll,
Ulrich A. Walker
Publication year - 2013
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/tdnp-v721
Subject(s) - medicine