Open AccessPhase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector
Author(s) -
Dawn E. Bowles,
Scott WJ McPhee,
Chengwen Li,
Steven J. Gray,
Jade J Samulski,
Angelique S Camp,
Juan Li,
Bing Wang,
Paul E. Monahan,
Joseph E. Rabinowitz,
Joshua C Grieger,
Lakshmanan Govindasamy,
Mavis AgbandjeMcKenna,
Xiao Xiao,
R. Jude Samulski
Publication year - 2012
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/k4e8-xw30
Subject(s) - duchenne muscular dystrophy , genetic enhancement , vector (molecular biology) , muscular dystrophy , medicine , phase (matter) , gene , biology , genetics , physics , recombinant dna , quantum mechanics