
Migalastat improves diarrhea in patients with Fabry disease: clinical-biomarker correlations from the phase 3 FACETS trial
Author(s) -
Raphael Schiffmann,
Daniel G. Bichet,
Ana Jovanović,
D.A. Hughes,
Roberto Giugliani,
Ulla FeldtRasmussen,
Suma Shankar,
Laura Barisoni,
Robert B. Colvin,
Charles Jennette,
Fred Holdbrook,
Andrew E. Mulberg,
Jeffrey P. Castelli,
Nina Skuban,
Jay Barth,
Kathy Nicholls
Publication year - 2018
Publication title -
carolina digital repository (university of north carolina at chapel hill)
Language(s) - English
DOI - 10.17615/3fkv-x213
Subject(s) - fabry disease , biomarker , medicine , diarrhea , clinical trial , oncology , disease , chemistry , biochemistry