RNA-targeted drugs for neuromuscular diseases
Author(s) -
Alessandra Ferlini,
Aurélie Goyenvalle,
Francesco Muntoni
Publication year - 2020
Publication title -
science
Language(s) - Uncategorized
Resource type - Journals
SCImago Journal Rank - 12.556
H-Index - 1186
eISSN - 1095-9203
pISSN - 0036-8075
DOI - 10.1126/science.aba4515
Subject(s) - rna , medicine , computational biology , pharmacology , biology , genetics , gene
Progress with antisense oligonucleotide therapies opens a path for future development
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