Open AccessDose-response relationships for enzyme replacement therapy with imiglucerase/alglucerase in patients with Gaucher disease type 1
Author(s) -
Gregory A. Grabowski,
Katherine Kacena,
J. Alexander Cole,
Carla E. M. Hollak,
Lin Zhang,
John Yee,
Pramod K. Mistry,
Ari Zimran,
Joel Charrow,
Stephan vom Dahl
Publication year - 2009
Publication title -
genetics in medicine
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 3.509
H-Index - 128
eISSN - 1530-0366
pISSN - 1098-3600
DOI - 10.1097/gim.0b013e31818e2c19
Subject(s) - enzyme replacement therapy , medicine , observational study , propensity score matching , disease , dosing
To determine whether enzyme therapy with imiglucerase/alglucerase demonstrates dose-response relationships with doses and disease parameters used in routine clinical practice for Gaucher disease type 1 patients.
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