Open AccessPopulation-based assessment of nusinersen efficacy in children with spinal muscular atrophy: a 3-year follow-up study
Author(s) -
Féline E. V. Scheijmans,
Inge Cuppen,
Ruben P.A. van Eijk,
Camiel A. Wijngaarde,
Marja Schoenmakers,
Danny R van der Woude,
Bart Bartels,
Esther S. Veldhoen,
Irene L B Oude Lansink,
Ewout J. N. Groen,
FayLynn Asselman,
Renske I. Wadman,
W. Ludo van der Pol
Publication year - 2022
Publication title -
brain communications
Language(s) - English
Resource type - Journals
ISSN - 2632-1297
DOI - 10.1093/braincomms/fcac269
Subject(s) - spinal muscular atrophy , medicine , cohort , population , natural history , neuromuscular disease , pediatrics , cohort study , motor function , adverse effect , physical therapy , atrophy , disease , physical medicine and rehabilitation , environmental health
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