Gene therapy targeting the blood–brain barrier improves neurological symptoms in a model of genetic MCT8 deficiency
Author(s) -
Sivaraj Mohana Sundaram,
Adriana Arrulo Pereira,
Helge MüllerFielitz,
Hannes Köpke,
Meri De Angelis,
Timo D. Müller,
Heike Heuer,
Jakob Körbelin,
Markus Krohn,
Jens Mittag,
Rubén Nogueiras,
Vincent Prévot,
Markus Schwaninger
Publication year - 2022
Publication title -
brain
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 5.142
H-Index - 336
eISSN - 1460-2156
pISSN - 0006-8950
DOI - 10.1093/brain/awac243
Subject(s) - monocarboxylate transporter , hormone , thyroid , blood–brain barrier , genetic enhancement , disease , medicine , endocrinology , bioinformatics , neuroscience , transporter , gene , psychology , central nervous system , biology , genetics
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