Gene and Cell Therapy for Muscular Dystrophies: Are We Getting There? | Zendy

Francesco Galli | Zendy; Laricia Bragg | Zendy; Linda Meggiolaro | Zendy; Maira Rossi | Zendy; Miriam Caffarini | Zendy; Naila Naz | Zendy; Sabrina Santoleri | Zendy; Giulio Cossu | Zendy

AI Assistant Blog Pricing

Home ZAIA Blog

Open Access

Gene and Cell Therapy for Muscular Dystrophies: Are We Getting There?

Author(s) -

Francesco Galli,

Laricia Bragg,

Linda Meggiolaro,

Maira Rossi,

Miriam Caffarini,

Naila Naz,

Sabrina Santoleri,

Giulio Cossu

Publication year - 2018

Publication title -

human gene therapy

Language(s) - English

Resource type - Journals

SCImago Journal Rank - 1.633

H-Index - 149

eISSN - 1557-7422

pISSN - 1043-0342

DOI - 10.1089/hum.2018.151

Subject(s) - genetic enhancement , muscular dystrophy , clinical trial , cell therapy , medicine , bioinformatics , gene , cell , biology , genetics

In the last few years, significant advances have occurred in the preclinical and clinical work toward gene and cell therapy for muscular dystrophy. At the time of this writing, several trials are ongoing and more are expected to start. It is thus a time of expectation, even though many hurdles remain and it is unclear whether they will be overcome with current strategies or if further improvements will be necessary.

The content you want is available to Zendy users.

Already have an account? Click here to sign in.

Having issues? You can contact us here

Accelerating Research