Open AccessPhase 1–2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B
Author(s) -
Pratima Chowdary,
Susan Shapiro,
Michael Makris,
Gillian Evans,
Sara Boyce,
Kate Talks,
Gerard Dolan,
Ulrike M. Reiss,
Mark Phillips,
Anne Riddell,
Maria R. Peralta,
Michelle Quaye,
David Patch,
Edward G. D. Tuddenham,
Allison Dane,
Marie Watissée,
Alison Long,
Amit C. Nathwani
Publication year - 2022
Publication title -
new england journal of medicine
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 19.889
H-Index - 1030
eISSN - 1533-4406
pISSN - 0028-4793
DOI - 10.1056/nejmoa2119913
Subject(s) - genetic enhancement , capsid , adeno associated virus , factor ix , virology , gene , medicine , virus , biology , genetics , recombinant dna , vector (molecular biology)
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