Efficacy of adeno-associated virus gene therapy in a MNGIE murine model enhanced by chronic exposure to nucleosides
Author(s) -
Ferran VilaJulià,
Raquel Cabrera-Pérez,
Yolanda Cámara,
Miguel MolinaBerenguer,
Silvia LopePiedrafita,
Michio Hirano,
Federico Mingozzi,
Javier TorresTorronteras,
Ramón Martí
Publication year - 2020
Publication title -
ebiomedicine
Language(s) - English
Resource type - Journals
ISSN - 2352-3964
DOI - 10.1016/j.ebiom.2020.103133
Subject(s) - adeno associated virus , genetic enhancement , phenotype , biology , nucleoside , knockout mouse , virus , medicine , immunology , gene , vector (molecular biology) , genetics , recombinant dna
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