Open AccessClinical experience of nusinersen in a broad spectrum of spinal muscular atrophy: A retrospective study
Author(s) -
Ae Ryoung Kim,
JongMok Lee,
Yu-Sun Min,
Hoseok Lee,
Dongsub Kim,
Su-Kyeong Hwang,
Soonhak Kwon,
Yun Jeong Lee
Publication year - 2020
Publication title -
annals of indian academy of neurology
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.427
H-Index - 31
eISSN - 1998-3549
pISSN - 0972-2327
DOI - 10.4103/aian.aian_524_20
Subject(s) - medicine , sma* , spinal muscular atrophy , adverse effect , surgery , quality of life (healthcare) , motor function , pediatrics , disease , physical medicine and rehabilitation , mathematics , nursing , combinatorics
Nusinersen has recently been approved and more widely used as first-line treatment of spinal muscular atrophy (SMA). This study aimed to evaluate the real-world experience of nusinersen use for patients with a broad spectrum of SMA.