Open AccessDecision-Making And Selection Bias in Four Observational Studies on Duchenne and Becker Muscular Dystrophy
Author(s) -
K. Naarding,
N. Doorenweerd,
Z. Koeks,
R. Hendriksen,
Kinita A. Chotkan,
Yvonne D. Krom,
I. de Groot,
C.S.M. Straathof,
Erik H. Niks,
H. Kan
Publication year - 2020
Publication title -
journal of neuromuscular diseases
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 1.366
H-Index - 23
eISSN - 2214-3602
pISSN - 2214-3599
DOI - 10.3233/jnd-200541
Subject(s) - observational study , medicine , duchenne muscular dystrophy , muscular dystrophy , physical therapy , natural history , cross sectional study , physical medicine and rehabilitation , pediatrics , pathology
Natural history data are essential for trial design in Duchenne (DMD) and Becker muscular dystrophy (BMD), but recruitment for observational studies can be challenging.