Open AccessProxy-Reported Quality of Life and Access to Nusinersen Among Patients with Spinal Muscular Atrophy in Saudi Arabia
Author(s) -
Yazed AlRuthia,
Ghadah S. Almuaythir,
Hala Alrasheed,
Wejdan R. Alsharif,
Mohamad-Hani Temsah,
Fahad Alsohime,
Ibrahim Sales,
Fahad A. Bashiri
Publication year - 2021
Publication title -
patient preference and adherence
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.885
H-Index - 48
ISSN - 1177-889X
DOI - 10.2147/ppa.s305849
Subject(s) - sma* , medicine , spinal muscular atrophy , visual analogue scale , quality of life (healthcare) , physical therapy , pediatrics , surgery , disease , nursing , mathematics , combinatorics
The recent approval of innovative therapies for spinal muscular atrophy (SMA), such as nusinersen, has brought hope to patients and their families.