P1546: ACTIVATE‐KIDST: MITAPIVAT IN CHILDREN WITH PYRUVATE KINASE DEFICIENCY WHO ARE REGULARLY TRANSFUSED
Author(s) -
Grace R. F.,
Tyler P. D.,
Little M.,
Kosinski P. A.,
Bey V.
Publication year - 2022
Publication title -
hemasphere
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.677
H-Index - 11
ISSN - 2572-9241
DOI - 10.1097/01.hs9.0000849040.78582.c7
Subject(s) - medicine , pyruvate kinase deficiency , splenectomy , pyruvate kinase , hemolysis , pediatrics , placebo , anemia , spleen , glycolysis , metabolism , alternative medicine , pathology
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