Open AccessPositive Effectiveness of Tafamidis in Delaying Disease Progression in Transthyretin Familial Amyloid Polyneuropathy up to 2 Years: An Analysis from the Transthyretin Amyloidosis Outcomes Survey (THAOS)
Author(s) -
Rajiv Mundayat,
Michelle Stewart,
José Alvir,
Sarah P. Short,
Moh Lim Ong,
Denis Keohane,
Denise Rill,
Marla B. Sultan
Publication year - 2018
Publication title -
neurology and therapy
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 1.296
H-Index - 19
eISSN - 2193-8253
pISSN - 2193-6536
DOI - 10.1007/s40120-018-0097-9
Subject(s) - medicine , transthyretin , amyloidosis , cohort , hazard ratio , polyneuropathy , gastroenterology , physical therapy , confidence interval
The effectiveness of tafamidis for the treatment of transthyretin familial amyloid polyneuropathy (TTR-FAP) was evaluated using data from the Transthyretin Amyloidosis Outcomes Survey (THAOS) registry.