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P1436: DEVELOPMENT OF A BETA‐GLOBIN GENE REPLACEMENT STRATEGY AS A THERAPEUTIC APPROACH FOR ΒETA‐THALASSEMIA
Author(s) -
Wienert B.,
Wallace K.,
Bandoro C.,
Churi A.,
Partridge J.,
Sharma R.,
Matern W.,
Treusch S.,
Dever D.
Publication year - 2022
Publication title -
hemasphere
Language(s) - English
Resource type - Journals
SCImago Journal Rank - 0.677
H-Index - 11
ISSN - 2572-9241
DOI - 10.1097/01.hs9.0000848600.72042.5d
Subject(s) - biology , genetics , gene , locus (genetics) , globin , thalassemia , microbiology and biotechnology